Expert Interview
Discussing Sarepta Therapeutics’ gene therapy, ELEVIDYS (delandistrogene moxeparvovec-rokl) and the recently announced results from the Phase 3 EMBARK study.
Ticker(s): SRPTInstitution: Duke University
- Former Co-Director of Duke Children's Neuromuscular Program & Professor of Neurology and Pediatrics at Duke, recently made a career change and is now exclusively focused on clinical trials.
- Treated hundreds of neuromuscular patients, including 150 DMD patients of all ages in 2023
- Actively involved in clinical research and many trials with a focus on pedicatric neuromuscular diseases; PI on multiple DMD studies including an Exon 53 skipping specific study.
Roughly how many patients do you treat per year for DMD?
Added By: sara_adminAre the results from the Phase 3 EMBARK study shocking to you?
Added By: sara_adminDo you believe ELEVIDYS shows clinical promise based on the results from the secondary endpoints in the EMBARK study?
Added By: sara_adminAre You Interested In These Questions?
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