A look at gene therapies in Sickle Cell disease including Vertex and CRISPR Therapeutics' CASGEVY (Exa-cel) and bluebird bio's LYFGENIA (lovotibeglogene autotemcel).

Executed on:Apr 30, 2024 1:00 PM EDT

Call Duration:30 minutes

Expert Profile

ExpertBlinded Expert

Institution: Cook Children's Physician NetworkPediatric Hematologist and Director the Bleeding Disorder Program and Hemophilia Treatment Center at Cook Children's
Manages 25 patients with Hemophilia B and 200 patients with SCD
Clinical interest in hemoglobinopathy including sickle cell disease, thalassemia and refractoy iron deficiency anemia; Research interest in sickle cell disease and cancer (febrile neutropenia), and iron deficiency anemia.

Interview Goal

On this call we will be discussing the potential and efficacy of gene therapies in patients with SCD.

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