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An updated look at Vertex & CRISPR's exa-cel in patients with sickle cell disease (SCD) and transfusion-dependent beta thalassemia (TDT)

Executed on:Sep 1, 2023 11:30 AM EDT
Call Duration:30 minutes

Expert Profile

ExpertBlinded Expert
Institution: Boston University
  • Professor of Medicine, Pediatrics, Pathology and Laboratory Medicine at Boston University
  • Treats 420 patients with sickle cell disease
  • Published 460+ articles and 3 textbooks on SCD and has a research focus on disorders of red blood cells

Interview Goal

On this call, we aim to discuss exagamglogene autotemcel (exa-cel) and the Phase 3 studies of exa-cel in patients with TDT(CLIMB THAL-111) and in patients with severe SCD (CLIMB SCD-121), which were presented at ASH 2022.

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